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ASO Therapy 10 24
Natasha and Joe's Wedding, April 15, 2024
2024 LGMD Lecture
FSHD Exercise and New Therapies
Riboflavin Deficiency SLC52A3 Variant
Case Reports RYR1, DMD, Congenital Myasthenia
Genetic Testing and Myalgia Workup
Progressive Teenage Fatigue
Early Fatigue in children
Gene Therapy Risks, AAV Vector
CMT, SORD
CLINICAL TRIAL UPDATES FOR LGMD (Part 2)
MAKING GENE THERAPY MORE VERSATILE FOR LGMD, 2023
Therapeutic Approaches for Dominantly Inherited LGMDs, 2023
CLINICAL TRIAL UPDATES for LGMD, 2023 (Part 1)
LGMD DIAGNOSIS AND CLINICAL CARE:
2023 MDA Conference: FDA Guidelines and Processes for Approval of Genetic therapies.
2023 MDA Conference: New Paradigms for Ultra Rare Genetic Diseases
2023 MDA Conference: Advances in Therapy for Mitochondrial Myopathies.
2023 MDA Conference: Gene therapy for Cardiac Disease featuring DMD
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